U.S. FDA Defers Action on Filing for AT-GAA in Late-onset Pompe Disease
By Dr. Matthew Watson
FDA Issues Deferred Action Letter on AT-GAA Regulatory Filing Due to the Inability to Conduct Required Manufacturing Site Inspection Prior to the PDUFA Action Date
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U.S. FDA Defers Action on Filing for AT-GAA in Late-onset Pompe Disease
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October 29th, 2022
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